NDF is an award-winning, California based nonprofit dedicated to improving the lives of people living with GNE Myopathy ( a genetic muscle-wasting disease) through advocacy, education, and scientific programs. NDF is the world’s largest nonprofit funder of Clinical research to pursue curative treatments, by working with leading the US and International Investigators. NDF is currently providing funding in the form of gifts and grants to organizations such as the NIH, Yale University, Nationwide Children’s Hospital, Hadassah Medical Center in Israel, and the Center for Neurology and Psychiatry (NMD) Japan. NDF is currently working on preclinical studies and some manufacturing to support an IND for AAV gene therapy clinical trials.
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