“Hope Lies in Dreams”—Ionis’s Stan Crooke and the First Drug for SMA Patients

3:30 PM - 4:30 PM (PDT), Monday, June 13, 2022 ・ Session Room 11A

Stan Crooke and his Ionis Pharmaceuticals team pioneered antisense drugs and developed the first medicine approved for patients suffering from spiral muscular atrophy (SMA).  The multidecade journey holds lessons for using antisense drugs against other diseases as well as the broader scientific and management practices critical for any company developing treatments for rare diseases that have no medicines yet.