Transformative therapies provide a significant, durable benefit and value for patient health outcomes, delivery of care, and overall health care spending. These therapies are aimed at serious and rare diseases where patients often have limited treatment options. Examples of transformative therapies include cellular and gene therapies, which are truly personalized medicines that target treatment to specific patient populations or subsets of patient populations.
Genome editing represents one of the most promising areas of biotechnology, with the potential for transformative breakthroughs in both human health and agriculture. Find important resources and background materials to better understand these groundbreaking innovations and what is needed to ensure that society can harness the full potential.